Exciting and encouraging news is making its way around the Friedreich's Ataxia (FA) community today.
Article highlights include:
"Researchers have successfully corrected a mutated frataxin gene that leads to reduced production of the frataxin (FTX) protein and development of disease in mice, according to new research.
This achievement provides new insight into laboratory methods to study the disease and supports the therapeutic potential of gene editing techniques to treat patients with Friedreich’s ataxia (FRDA) in the future."
"In recent years, researchers have developed gene editing techniques that allow them to repair, replace, or modify specific genes. This ability has great therapeutic potential for diseases caused by gene mutations, such as Friedreich’s ataxia."
For the full article, click here.
I personally believe that our cure will come in the form of gene therapy/editing. Until then, we will just keep trying to slow or stop disease progression with a cocktail of treatment therapies. Hopefully more exciting updated like this will soon follow! Keep the faith, Team!